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    Adenine base editing of the polyadenylation signal for targeted genetic therapy in facioscapulohumeral muscular dystrophy.

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    Authors
    Šikrová, Darina
    Cadar, Vlad A
    Ariyurek, Yavuz
    Laros, Jeroen F J
    Balog, Judit
    van der Maarel, Silvère M
    Type
    Article
    Language
    en
    
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    Title
    Adenine base editing of the polyadenylation signal for targeted genetic therapy in facioscapulohumeral muscular dystrophy.
    Published in
    Molecular Ther Nucleid Acids 2021; 25:342-54
    DOI
    10.1016/j.omtn.2021.05.020
    PMID
    34484861
    URI
    http://hdl.handle.net/10029/625283
    ae974a485f413a2113503eed53cd6c53
    10.1016/j.omtn.2021.05.020
    Scopus Count
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