Adenine base editing of the polyadenylation signal for targeted genetic therapy in facioscapulohumeral muscular dystrophy.
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Authors
Šikrová, DarinaCadar, Vlad A
Ariyurek, Yavuz
Laros, Jeroen F J
Balog, Judit
van der Maarel, Silvère M
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ArticleLanguage
en
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Show full item recordTitle
Adenine base editing of the polyadenylation signal for targeted genetic therapy in facioscapulohumeral muscular dystrophy.Published in
Molecular Ther Nucleid Acids 2021; 25:342-54PMID
34484861ae974a485f413a2113503eed53cd6c53
10.1016/j.omtn.2021.05.020
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